In the medicine field gene therapy (also called human gene transfer) is the therapeutic delivery of nucleic acid into a patient's cells as a drug to treat disease.A genetic disorder is a genetic problem caused by one or more abnormalities formed in the genome.
This report aims to provide a comprehensive presentation of the global market for Gene Therapy for Inherited Genetic Disorders, with both quantitative and qualitative analysis, to help readers develop business/growth strategies, assess the market competitive situation, analyze their position in the current marketplace, and make informed business decisions regarding Gene Therapy for Inherited Genetic Disorders. This report contains market size and forecasts of Gene Therapy for Inherited Genetic Disorders in global, including the following market information:
Global Gene Therapy for Inherited Genetic Disorders Market Revenue, 2018-2023, 2024-2030, ($ millions)
Global top five companies in 2022 (%)
The global Gene Therapy for Inherited Genetic Disorders market was valued at US$ million in 2022 and is projected to reach US$ million by 2029, at a CAGR of % during the forecast period. The influence of COVID-19 and the Russia-Ukraine War were considered while estimating market sizes.
Gene therapy has the potential to cure inherited diseases that cannot be cured using conventional drugs. It is being increasingly adopted in clinical trials because of its high efficacy and safety towards the treatment of inherited genetic disorders.
We surveyed the Gene Therapy for Inherited Genetic Disorders companies, and industry experts on this industry, involving the revenue, demand, product type, recent developments and plans, industry trends, drivers, challenges, obstacles, and potential risks.
Total Market by Segment:
Global Gene Therapy for Inherited Genetic Disorders Market, by Type, 2018-2023, 2024-2030 ($ millions)
Global Gene Therapy for Inherited Genetic Disorders Market Segment Percentages, by Type, 2022 (%)
Eye Disorders
Hematological Disorders
Central Nervous System Disorders
Muscular Disorders
Others
Global Gene Therapy for Inherited Genetic Disorders Market, by Application, 2018-2023, 2024-2030 ($ millions)
Global Gene Therapy for Inherited Genetic Disorders Market Segment Percentages, by Application, 2022 (%)
Hospital
Clinic
Research Institute
Others
Global Gene Therapy for Inherited Genetic Disorders Market, By Region and Country, 2018-2023, 2024-2030 ($ Millions)
Global Gene Therapy for Inherited Genetic Disorders Market Segment Percentages, By Region and Country, 2022 (%)
North America
US
Canada
Mexico
Europe
Germany
France
U.K.
Italy
Russia
Nordic Countries
Benelux
Rest of Europe
Asia
China
Japan
South Korea
Southeast Asia
India
Rest of Asia
South America
Brazil
Argentina
Rest of South America
Middle East & Africa
Turkey
Israel
Saudi Arabia
UAE
Rest of Middle East & Africa
Competitor Analysis
The report also provides analysis of leading market participants including:
Key companies Gene Therapy for Inherited Genetic Disorders revenues in global market, 2018-2023 (estimated), ($ millions)
Key companies Gene Therapy for Inherited Genetic Disorders revenues share in global market, 2022 (%)
Further, the report presents profiles of competitors in the market, key players include:
BioMarin Pharmaceutical Inc.
bluebird bio Inc.
Novartis AG
Orchard Therapeutics Plc
Spark Therapeutics Inc.
Outline of Major Chapters:
Chapter 1: Introduces the definition of Gene Therapy for Inherited Genetic Disorders, market overview.
Chapter 2: Global Gene Therapy for Inherited Genetic Disorders market size in revenue.
Chapter 3: Detailed analysis of Gene Therapy for Inherited Genetic Disorders company competitive landscape, revenue and market share, latest development plan, merger, and acquisition information, etc.
Chapter 4: Provides the analysis of various market segments by type, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different market segments.
Chapter 5: Provides the analysis of various market segments by application, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different downstream markets.
Chapter 6: Sales of Gene Therapy for Inherited Genetic Disorders in regional level and country level. It provides a quantitative analysis of the market size and development potential of each region and its main countries and introduces the market development, future development prospects, market space of each country in the world.
Chapter 7: Provides profiles of key players, introducing the basic situation of the main companies in the market in detail, including product sales, revenue, price, gross margin, product introduction, recent development, etc.
Chapter 8: The main points and conclusions of the report.
TABLE OF CONTENTS
1 Introduction to Research & Analysis Reports
1.1 Gene Therapy for Inherited Genetic Disorders Market Definition
1.2 Market Segments
1.2.1 Market by Type
1.2.2 Market by Application
1.3 Global Gene Therapy for Inherited Genetic Disorders Market Overview
1.4 Features & Benefits of This Report
1.5 Methodology & Sources of Information
1.5.1 Research Methodology
1.5.2 Research Process
1.5.3 Base Year
1.5.4 Report Assumptions & Caveats
2 Global Gene Therapy for Inherited Genetic Disorders Overall Market Size
2.1 Global Gene Therapy for Inherited Genetic Disorders Market Size: 2022 VS 2030
2.2 Global Gene Therapy for Inherited Genetic Disorders Market Size, Prospects & Forecasts: 2018-2030
2.3 Key Market Trends, Opportunity, Drivers and Restraints
2.3.1 Market Opportunities & Trends
2.3.2 Market Drivers
2.3.3 Market Restraints
3 Company Landscape
3.1 Top Gene Therapy for Inherited Genetic Disorders Players in Global Market
3.2 Top Global Gene Therapy for Inherited Genetic Disorders Companies Ranked by Revenue
3.3 Global Gene Therapy for Inherited Genetic Disorders Revenue by Companies
3.4 Top 3 and Top 5 Gene Therapy for Inherited Genetic Disorders Companies in Global Market, by Revenue in 2022
3.5 Global Companies Gene Therapy for Inherited Genetic Disorders Product Type
3.6 Tier 1, Tier 2 and Tier 3 Gene Therapy for Inherited Genetic Disorders Players in Global Market
3.6.1 List of Global Tier 1 Gene Therapy for Inherited Genetic Disorders Companies
3.6.2 List of Global Tier 2 and Tier 3 Gene Therapy for Inherited Genetic Disorders Companies
4 Market Sights by Product
4.1 Overview
4.1.1 By Type - Global Gene Therapy for Inherited Genetic Disorders Market Size Markets, 2022 & 2030
4.1.2 Eye Disorders
4.1.3 Hematological Disorders
4.1.4 Central Nervous System Disorders
4.1.5 Muscular Disorders
4.1.6 Others
4.2 By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue & Forecasts
4.2.1 By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2023
4.2.2 By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2024-2030
4.2.3 By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
5 Sights by Application
5.1 Overview
5.1.1 By Application - Global Gene Therapy for Inherited Genetic Disorders Market Size, 2022 & 2030
5.1.2 Hospital
5.1.3 Clinic
5.1.4 Research Institute
5.1.5 Others
5.2 By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue & Forecasts
5.2.1 By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2023
5.2.2 By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2024-2030
5.2.3 By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
6 Sights by Region
6.1 By Region - Global Gene Therapy for Inherited Genetic Disorders Market Size, 2022 & 2030
6.2 By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue & Forecasts
6.2.1 By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2023
6.2.2 By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue, 2024-2030
6.2.3 By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
6.3 North America
6.3.1 By Country - North America Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030
6.3.2 US Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.3.3 Canada Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.3.4 Mexico Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4 Europe
6.4.1 By Country - Europe Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030
6.4.2 Germany Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.3 France Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.4 U.K. Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.5 Italy Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.6 Russia Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.7 Nordic Countries Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.4.8 Benelux Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.5 Asia
6.5.1 By Region - Asia Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030
6.5.2 China Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.5.3 Japan Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.5.4 South Korea Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.5.5 Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.5.6 India Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.6 South America
6.6.1 By Country - South America Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030
6.6.2 Brazil Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.6.3 Argentina Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.7 Middle East & Africa
6.7.1 By Country - Middle East & Africa Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030
6.7.2 Turkey Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.7.3 Israel Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.7.4 Saudi Arabia Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
6.7.5 UAE Gene Therapy for Inherited Genetic Disorders Market Size, 2018-2030
7 Gene Therapy for Inherited Genetic Disorders Companies Profiles
7.1 BioMarin Pharmaceutical Inc.
7.1.1 BioMarin Pharmaceutical Inc. Company Summary
7.1.2 BioMarin Pharmaceutical Inc. Business Overview
7.1.3 BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Major Product Offerings
7.1.4 BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Revenue in Global Market (2018-2023)
7.1.5 BioMarin Pharmaceutical Inc. Key News & Latest Developments
7.2 bluebird bio Inc.
7.2.1 bluebird bio Inc. Company Summary
7.2.2 bluebird bio Inc. Business Overview
7.2.3 bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Major Product Offerings
7.2.4 bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Revenue in Global Market (2018-2023)
7.2.5 bluebird bio Inc. Key News & Latest Developments
7.3 Novartis AG
7.3.1 Novartis AG Company Summary
7.3.2 Novartis AG Business Overview
7.3.3 Novartis AG Gene Therapy for Inherited Genetic Disorders Major Product Offerings
7.3.4 Novartis AG Gene Therapy for Inherited Genetic Disorders Revenue in Global Market (2018-2023)
7.3.5 Novartis AG Key News & Latest Developments
7.4 Orchard Therapeutics Plc
7.4.1 Orchard Therapeutics Plc Company Summary
7.4.2 Orchard Therapeutics Plc Business Overview
7.4.3 Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Major Product Offerings
7.4.4 Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Revenue in Global Market (2018-2023)
7.4.5 Orchard Therapeutics Plc Key News & Latest Developments
7.5 Spark Therapeutics Inc.
7.5.1 Spark Therapeutics Inc. Company Summary
7.5.2 Spark Therapeutics Inc. Business Overview
7.5.3 Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Major Product Offerings
7.5.4 Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Revenue in Global Market (2018-2023)
7.5.5 Spark Therapeutics Inc. Key News & Latest Developments
8 Conclusion
9 Appendix
9.1 Note
9.2 Examples of Clients
9.3 Disclaimer
LIST OF TABLES & FIGURES
List of Tables
Table 1. Gene Therapy for Inherited Genetic Disorders Market Opportunities & Trends in Global Market
Table 2. Gene Therapy for Inherited Genetic Disorders Market Drivers in Global Market
Table 3. Gene Therapy for Inherited Genetic Disorders Market Restraints in Global Market
Table 4. Key Players of Gene Therapy for Inherited Genetic Disorders in Global Market
Table 5. Top Gene Therapy for Inherited Genetic Disorders Players in Global Market, Ranking by Revenue (2022)
Table 6. Global Gene Therapy for Inherited Genetic Disorders Revenue by Companies, (US$, Mn), 2018-2023
Table 7. Global Gene Therapy for Inherited Genetic Disorders Revenue Share by Companies, 2018-2023
Table 8. Global Companies Gene Therapy for Inherited Genetic Disorders Product Type
Table 9. List of Global Tier 1 Gene Therapy for Inherited Genetic Disorders Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 10. List of Global Tier 2 and Tier 3 Gene Therapy for Inherited Genetic Disorders Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 11. By Type ? Global Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2022 & 2030
Table 12. By Type - Gene Therapy for Inherited Genetic Disorders Revenue in Global (US$, Mn), 2018-2023
Table 13. By Type - Gene Therapy for Inherited Genetic Disorders Revenue in Global (US$, Mn), 2024-2030
Table 14. By Application ? Global Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2022 & 2030
Table 15. By Application - Gene Therapy for Inherited Genetic Disorders Revenue in Global (US$, Mn), 2018-2023
Table 16. By Application - Gene Therapy for Inherited Genetic Disorders Revenue in Global (US$, Mn), 2024-2030
Table 17. By Region ? Global Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2022 & 2030
Table 18. By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn), 2018-2023
Table 19. By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn), 2024-2030
Table 20. By Country - North America Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2023
Table 21. By Country - North America Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2024-2030
Table 22. By Country - Europe Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2023
Table 23. By Country - Europe Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2024-2030
Table 24. By Region - Asia Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2023
Table 25. By Region - Asia Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2024-2030
Table 26. By Country - South America Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2023
Table 27. By Country - South America Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2024-2030
Table 28. By Country - Middle East & Africa Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2023
Table 29. By Country - Middle East & Africa Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2024-2030
Table 30. BioMarin Pharmaceutical Inc. Company Summary
Table 31. BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Product Offerings
Table 32. BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn) & (2018-2023)
Table 33. BioMarin Pharmaceutical Inc. Key News & Latest Developments
Table 34. bluebird bio Inc. Company Summary
Table 35. bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Product Offerings
Table 36. bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn) & (2018-2023)
Table 37. bluebird bio Inc. Key News & Latest Developments
Table 38. Novartis AG Company Summary
Table 39. Novartis AG Gene Therapy for Inherited Genetic Disorders Product Offerings
Table 40. Novartis AG Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn) & (2018-2023)
Table 41. Novartis AG Key News & Latest Developments
Table 42. Orchard Therapeutics Plc Company Summary
Table 43. Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Product Offerings
Table 44. Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn) & (2018-2023)
Table 45. Orchard Therapeutics Plc Key News & Latest Developments
Table 46. Spark Therapeutics Inc. Company Summary
Table 47. Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Product Offerings
Table 48. Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Revenue (US$, Mn) & (2018-2023)
Table 49. Spark Therapeutics Inc. Key News & Latest Developments
List of Figures
Figure 1. Gene Therapy for Inherited Genetic Disorders Segment by Type in 2022
Figure 2. Gene Therapy for Inherited Genetic Disorders Segment by Application in 2022
Figure 3. Global Gene Therapy for Inherited Genetic Disorders Market Overview: 2022
Figure 4. Key Caveats
Figure 5. Global Gene Therapy for Inherited Genetic Disorders Market Size: 2022 VS 2030 (US$, Mn)
Figure 6. Global Gene Therapy for Inherited Genetic Disorders Revenue, 2018-2030 (US$, Mn)
Figure 7. The Top 3 and 5 Players Market Share by Gene Therapy for Inherited Genetic Disorders Revenue in 2022
Figure 8. By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 9. By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 10. By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2022 & 2030
Figure 11. By Type - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 12. By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2022 & 2030
Figure 13. By Application - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 14. By Region - Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 15. By Country - North America Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 16. US Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 17. Canada Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 18. Mexico Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 19. By Country - Europe Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 20. Germany Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 21. France Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 22. U.K. Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 23. Italy Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 24. Russia Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 25. Nordic Countries Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 26. Benelux Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 27. By Region - Asia Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 28. China Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 29. Japan Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 30. South Korea Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 31. Southeast Asia Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 32. India Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 33. By Country - South America Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 34. Brazil Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 35. Argentina Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 36. By Country - Middle East & Africa Gene Therapy for Inherited Genetic Disorders Revenue Market Share, 2018-2030
Figure 37. Turkey Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 38. Israel Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 39. Saudi Arabia Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 40. UAE Gene Therapy for Inherited Genetic Disorders Revenue, (US$, Mn), 2018-2030
Figure 41. BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 42. bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 43. Novartis AG Gene Therapy for Inherited Genetic Disorders Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 44. Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 45. Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
