Hemophilia is a rare bleeding disorder in which the blood does not clot normally. Hemophilia is a monogenic disease (a disease that is caused by a genetic defect in a single gene). There are two types of hemophilia caused by mutations in genes that encode protein factors which help the blood clot and stop bleeding when blood vessels are injured. Individuals with hemophilia experience bleeding episodes after injuries and spontaneous bleeding episodes that often lead to joint disease such as arthritis. The most frequent forms of hemophilia affect males.
This report aims to provide a comprehensive presentation of the global market for Hemophilia Gene Therapy, with both quantitative and qualitative analysis, to help readers develop business/growth strategies, assess the market competitive situation, analyze their position in the current marketplace, and make informed business decisions regarding Hemophilia Gene Therapy. This report contains market size and forecasts of Hemophilia Gene Therapy in global, including the following market information:
Global Hemophilia Gene Therapy Market Revenue, 2018-2023, 2024-2029, ($ millions)
Global top five companies in 2022 (%)
The global Hemophilia Gene Therapy market was valued at US$ million in 2022 and is projected to reach US$ million by 2029, at a CAGR of % during the forecast period. The influence of COVID-19 and the Russia-Ukraine War were considered while estimating market sizes.
Global Hemophilia Gene Therapy key players include Spark Therapeutics, Ultragenyx, Shire PLC, Sangamo Therapeutics, etc.
We surveyed the Hemophilia Gene Therapy companies, and industry experts on this industry, involving the revenue, demand, product type, recent developments and plans, industry trends, drivers, challenges, obstacles, and potential risks.
Total Market by Segment:
Global Hemophilia Gene Therapy Market, by Type, 2018-2023, 2024-2029 ($ millions)
Global Hemophilia Gene Therapy Market Segment Percentages, by Type, 2022 (%)
Hemophilia A
Hemophilia B
Global Hemophilia Gene Therapy Market, by Application, 2018-2023, 2024-2029 ($ millions)
Global Hemophilia Gene Therapy Market Segment Percentages, by Application, 2022 (%)
Hemophilia A Gene Therapy
Hemophilia B Gene Therapy
Global Hemophilia Gene Therapy Market, By Region and Country, 2018-2023, 2024-2029 ($ Millions)
Global Hemophilia Gene Therapy Market Segment Percentages, By Region and Country, 2022 (%)
North America
US
Canada
Mexico
Europe
Germany
France
U.K.
Italy
Russia
Nordic Countries
Benelux
Rest of Europe
Asia
China
Japan
South Korea
Southeast Asia
India
Rest of Asia
South America
Brazil
Argentina
Rest of South America
Middle East & Africa
Turkey
Israel
Saudi Arabia
UAE
Rest of Middle East & Africa
Competitor Analysis
The report also provides analysis of leading market participants including:
Key companies Hemophilia Gene Therapy revenues in global market, 2018-2023 (estimated), ($ millions)
Key companies Hemophilia Gene Therapy revenues share in global market, 2022 (%)
Further, the report presents profiles of competitors in the market, key players include:
Spark Therapeutics
Ultragenyx
Shire PLC
Sangamo Therapeutics
Bioverativ
BioMarin
uniQure
Freeline Therapeutics
Outline of Major Chapters:
Chapter 1: Introduces the definition of Hemophilia Gene Therapy, market overview.
Chapter 2: Global Hemophilia Gene Therapy market size in revenue.
Chapter 3: Detailed analysis of Hemophilia Gene Therapy company competitive landscape, revenue and market share, latest development plan, merger, and acquisition information, etc.
Chapter 4: Provides the analysis of various market segments by type, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different market segments.
Chapter 5: Provides the analysis of various market segments by application, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different downstream markets.
Chapter 6: Sales of Hemophilia Gene Therapy in regional level and country level. It provides a quantitative analysis of the market size and development potential of each region and its main countries and introduces the market development, future development prospects, market space of each country in the world.
Chapter 7: Provides profiles of key players, introducing the basic situation of the main companies in the market in detail, including product sales, revenue, price, gross margin, product introduction, recent development, etc.
Chapter 8: The main points and conclusions of the report.
TABLE OF CONTENTS
1 Introduction to Research & Analysis Reports
1.1 Hemophilia Gene Therapy Market Definition
1.2 Market Segments
1.2.1 Market by Type
1.2.2 Market by Application
1.3 Global Hemophilia Gene Therapy Market Overview
1.4 Features & Benefits of This Report
1.5 Methodology & Sources of Information
1.5.1 Research Methodology
1.5.2 Research Process
1.5.3 Base Year
1.5.4 Report Assumptions & Caveats
2 Global Hemophilia Gene Therapy Overall Market Size
2.1 Global Hemophilia Gene Therapy Market Size: 2022 VS 2029
2.2 Global Hemophilia Gene Therapy Market Size, Prospects & Forecasts: 2018-2029
2.3 Key Market Trends, Opportunity, Drivers and Restraints
2.3.1 Market Opportunities & Trends
2.3.2 Market Drivers
2.3.3 Market Restraints
3 Company Landscape
3.1 Top Hemophilia Gene Therapy Players in Global Market
3.2 Top Global Hemophilia Gene Therapy Companies Ranked by Revenue
3.3 Global Hemophilia Gene Therapy Revenue by Companies
3.4 Top 3 and Top 5 Hemophilia Gene Therapy Companies in Global Market, by Revenue in 2022
3.5 Global Companies Hemophilia Gene Therapy Product Type
3.6 Tier 1, Tier 2 and Tier 3 Hemophilia Gene Therapy Players in Global Market
3.6.1 List of Global Tier 1 Hemophilia Gene Therapy Companies
3.6.2 List of Global Tier 2 and Tier 3 Hemophilia Gene Therapy Companies
4 Market Sights by Product
4.1 Overview
4.1.1 By Type - Global Hemophilia Gene Therapy Market Size Markets, 2022 & 2029
4.1.2 Hemophilia A
4.1.3 Hemophilia B
4.2 By Type - Global Hemophilia Gene Therapy Revenue & Forecasts
4.2.1 By Type - Global Hemophilia Gene Therapy Revenue, 2018-2023
4.2.2 By Type - Global Hemophilia Gene Therapy Revenue, 2024-2029
4.2.3 By Type - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
5 Sights by Application
5.1 Overview
5.1.1 By Application - Global Hemophilia Gene Therapy Market Size, 2022 & 2029
5.1.2 Hemophilia A Gene Therapy
5.1.3 Hemophilia B Gene Therapy
5.2 By Application - Global Hemophilia Gene Therapy Revenue & Forecasts
5.2.1 By Application - Global Hemophilia Gene Therapy Revenue, 2018-2023
5.2.2 By Application - Global Hemophilia Gene Therapy Revenue, 2024-2029
5.2.3 By Application - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
6 Sights by Region
6.1 By Region - Global Hemophilia Gene Therapy Market Size, 2022 & 2029
6.2 By Region - Global Hemophilia Gene Therapy Revenue & Forecasts
6.2.1 By Region - Global Hemophilia Gene Therapy Revenue, 2018-2023
6.2.2 By Region - Global Hemophilia Gene Therapy Revenue, 2024-2029
6.2.3 By Region - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
6.3 North America
6.3.1 By Country - North America Hemophilia Gene Therapy Revenue, 2018-2029
6.3.2 US Hemophilia Gene Therapy Market Size, 2018-2029
6.3.3 Canada Hemophilia Gene Therapy Market Size, 2018-2029
6.3.4 Mexico Hemophilia Gene Therapy Market Size, 2018-2029
6.4 Europe
6.4.1 By Country - Europe Hemophilia Gene Therapy Revenue, 2018-2029
6.4.2 Germany Hemophilia Gene Therapy Market Size, 2018-2029
6.4.3 France Hemophilia Gene Therapy Market Size, 2018-2029
6.4.4 U.K. Hemophilia Gene Therapy Market Size, 2018-2029
6.4.5 Italy Hemophilia Gene Therapy Market Size, 2018-2029
6.4.6 Russia Hemophilia Gene Therapy Market Size, 2018-2029
6.4.7 Nordic Countries Hemophilia Gene Therapy Market Size, 2018-2029
6.4.8 Benelux Hemophilia Gene Therapy Market Size, 2018-2029
6.5 Asia
6.5.1 By Region - Asia Hemophilia Gene Therapy Revenue, 2018-2029
6.5.2 China Hemophilia Gene Therapy Market Size, 2018-2029
6.5.3 Japan Hemophilia Gene Therapy Market Size, 2018-2029
6.5.4 South Korea Hemophilia Gene Therapy Market Size, 2018-2029
6.5.5 Southeast Asia Hemophilia Gene Therapy Market Size, 2018-2029
6.5.6 India Hemophilia Gene Therapy Market Size, 2018-2029
6.6 South America
6.6.1 By Country - South America Hemophilia Gene Therapy Revenue, 2018-2029
6.6.2 Brazil Hemophilia Gene Therapy Market Size, 2018-2029
6.6.3 Argentina Hemophilia Gene Therapy Market Size, 2018-2029
6.7 Middle East & Africa
6.7.1 By Country - Middle East & Africa Hemophilia Gene Therapy Revenue, 2018-2029
6.7.2 Turkey Hemophilia Gene Therapy Market Size, 2018-2029
6.7.3 Israel Hemophilia Gene Therapy Market Size, 2018-2029
6.7.4 Saudi Arabia Hemophilia Gene Therapy Market Size, 2018-2029
6.7.5 UAE Hemophilia Gene Therapy Market Size, 2018-2029
7 Hemophilia Gene Therapy Companies Profiles
7.1 Spark Therapeutics
7.1.1 Spark Therapeutics Company Summary
7.1.2 Spark Therapeutics Business Overview
7.1.3 Spark Therapeutics Hemophilia Gene Therapy Major Product Offerings
7.1.4 Spark Therapeutics Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.1.5 Spark Therapeutics Key News & Latest Developments
7.2 Ultragenyx
7.2.1 Ultragenyx Company Summary
7.2.2 Ultragenyx Business Overview
7.2.3 Ultragenyx Hemophilia Gene Therapy Major Product Offerings
7.2.4 Ultragenyx Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.2.5 Ultragenyx Key News & Latest Developments
7.3 Shire PLC
7.3.1 Shire PLC Company Summary
7.3.2 Shire PLC Business Overview
7.3.3 Shire PLC Hemophilia Gene Therapy Major Product Offerings
7.3.4 Shire PLC Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.3.5 Shire PLC Key News & Latest Developments
7.4 Sangamo Therapeutics
7.4.1 Sangamo Therapeutics Company Summary
7.4.2 Sangamo Therapeutics Business Overview
7.4.3 Sangamo Therapeutics Hemophilia Gene Therapy Major Product Offerings
7.4.4 Sangamo Therapeutics Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.4.5 Sangamo Therapeutics Key News & Latest Developments
7.5 Bioverativ
7.5.1 Bioverativ Company Summary
7.5.2 Bioverativ Business Overview
7.5.3 Bioverativ Hemophilia Gene Therapy Major Product Offerings
7.5.4 Bioverativ Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.5.5 Bioverativ Key News & Latest Developments
7.6 BioMarin
7.6.1 BioMarin Company Summary
7.6.2 BioMarin Business Overview
7.6.3 BioMarin Hemophilia Gene Therapy Major Product Offerings
7.6.4 BioMarin Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.6.5 BioMarin Key News & Latest Developments
7.7 uniQure
7.7.1 uniQure Company Summary
7.7.2 uniQure Business Overview
7.7.3 uniQure Hemophilia Gene Therapy Major Product Offerings
7.7.4 uniQure Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.7.5 uniQure Key News & Latest Developments
7.8 Freeline Therapeutics
7.8.1 Freeline Therapeutics Company Summary
7.8.2 Freeline Therapeutics Business Overview
7.8.3 Freeline Therapeutics Hemophilia Gene Therapy Major Product Offerings
7.8.4 Freeline Therapeutics Hemophilia Gene Therapy Revenue in Global Market (2018-2023)
7.8.5 Freeline Therapeutics Key News & Latest Developments
8 Conclusion
9 Appendix
9.1 Note
9.2 Examples of Clients
9.3 Disclaimer
LIST OF TABLES & FIGURES
List of Tables
Table 1. Hemophilia Gene Therapy Market Opportunities & Trends in Global Market
Table 2. Hemophilia Gene Therapy Market Drivers in Global Market
Table 3. Hemophilia Gene Therapy Market Restraints in Global Market
Table 4. Key Players of Hemophilia Gene Therapy in Global Market
Table 5. Top Hemophilia Gene Therapy Players in Global Market, Ranking by Revenue (2022)
Table 6. Global Hemophilia Gene Therapy Revenue by Companies, (US$, Mn), 2018-2023
Table 7. Global Hemophilia Gene Therapy Revenue Share by Companies, 2018-2023
Table 8. Global Companies Hemophilia Gene Therapy Product Type
Table 9. List of Global Tier 1 Hemophilia Gene Therapy Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 10. List of Global Tier 2 and Tier 3 Hemophilia Gene Therapy Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 11. By Type ? Global Hemophilia Gene Therapy Revenue, (US$, Mn), 2022 & 2029
Table 12. By Type - Hemophilia Gene Therapy Revenue in Global (US$, Mn), 2018-2023
Table 13. By Type - Hemophilia Gene Therapy Revenue in Global (US$, Mn), 2024-2029
Table 14. By Application ? Global Hemophilia Gene Therapy Revenue, (US$, Mn), 2022 & 2029
Table 15. By Application - Hemophilia Gene Therapy Revenue in Global (US$, Mn), 2018-2023
Table 16. By Application - Hemophilia Gene Therapy Revenue in Global (US$, Mn), 2024-2029
Table 17. By Region ? Global Hemophilia Gene Therapy Revenue, (US$, Mn), 2022 & 2029
Table 18. By Region - Global Hemophilia Gene Therapy Revenue (US$, Mn), 2018-2023
Table 19. By Region - Global Hemophilia Gene Therapy Revenue (US$, Mn), 2024-2029
Table 20. By Country - North America Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2023
Table 21. By Country - North America Hemophilia Gene Therapy Revenue, (US$, Mn), 2024-2029
Table 22. By Country - Europe Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2023
Table 23. By Country - Europe Hemophilia Gene Therapy Revenue, (US$, Mn), 2024-2029
Table 24. By Region - Asia Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2023
Table 25. By Region - Asia Hemophilia Gene Therapy Revenue, (US$, Mn), 2024-2029
Table 26. By Country - South America Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2023
Table 27. By Country - South America Hemophilia Gene Therapy Revenue, (US$, Mn), 2024-2029
Table 28. By Country - Middle East & Africa Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2023
Table 29. By Country - Middle East & Africa Hemophilia Gene Therapy Revenue, (US$, Mn), 2024-2029
Table 30. Spark Therapeutics Company Summary
Table 31. Spark Therapeutics Hemophilia Gene Therapy Product Offerings
Table 32. Spark Therapeutics Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 33. Spark Therapeutics Key News & Latest Developments
Table 34. Ultragenyx Company Summary
Table 35. Ultragenyx Hemophilia Gene Therapy Product Offerings
Table 36. Ultragenyx Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 37. Ultragenyx Key News & Latest Developments
Table 38. Shire PLC Company Summary
Table 39. Shire PLC Hemophilia Gene Therapy Product Offerings
Table 40. Shire PLC Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 41. Shire PLC Key News & Latest Developments
Table 42. Sangamo Therapeutics Company Summary
Table 43. Sangamo Therapeutics Hemophilia Gene Therapy Product Offerings
Table 44. Sangamo Therapeutics Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 45. Sangamo Therapeutics Key News & Latest Developments
Table 46. Bioverativ Company Summary
Table 47. Bioverativ Hemophilia Gene Therapy Product Offerings
Table 48. Bioverativ Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 49. Bioverativ Key News & Latest Developments
Table 50. BioMarin Company Summary
Table 51. BioMarin Hemophilia Gene Therapy Product Offerings
Table 52. BioMarin Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 53. BioMarin Key News & Latest Developments
Table 54. uniQure Company Summary
Table 55. uniQure Hemophilia Gene Therapy Product Offerings
Table 56. uniQure Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 57. uniQure Key News & Latest Developments
Table 58. Freeline Therapeutics Company Summary
Table 59. Freeline Therapeutics Hemophilia Gene Therapy Product Offerings
Table 60. Freeline Therapeutics Hemophilia Gene Therapy Revenue (US$, Mn) & (2018-2023)
Table 61. Freeline Therapeutics Key News & Latest Developments
List of Figures
Figure 1. Hemophilia Gene Therapy Segment by Type in 2022
Figure 2. Hemophilia Gene Therapy Segment by Application in 2022
Figure 3. Global Hemophilia Gene Therapy Market Overview: 2022
Figure 4. Key Caveats
Figure 5. Global Hemophilia Gene Therapy Market Size: 2022 VS 2029 (US$, Mn)
Figure 6. Global Hemophilia Gene Therapy Revenue, 2018-2029 (US$, Mn)
Figure 7. The Top 3 and 5 Players Market Share by Hemophilia Gene Therapy Revenue in 2022
Figure 8. By Type - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 9. By Application - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 10. By Type - Global Hemophilia Gene Therapy Revenue, (US$, Mn), 2022 & 2029
Figure 11. By Type - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 12. By Application - Global Hemophilia Gene Therapy Revenue, (US$, Mn), 2022 & 2029
Figure 13. By Application - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 14. By Region - Global Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 15. By Country - North America Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 16. US Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 17. Canada Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 18. Mexico Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 19. By Country - Europe Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 20. Germany Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 21. France Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 22. U.K. Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 23. Italy Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 24. Russia Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 25. Nordic Countries Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 26. Benelux Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 27. By Region - Asia Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 28. China Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 29. Japan Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 30. South Korea Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 31. Southeast Asia Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 32. India Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 33. By Country - South America Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 34. Brazil Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 35. Argentina Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 36. By Country - Middle East & Africa Hemophilia Gene Therapy Revenue Market Share, 2018-2029
Figure 37. Turkey Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 38. Israel Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 39. Saudi Arabia Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 40. UAE Hemophilia Gene Therapy Revenue, (US$, Mn), 2018-2029
Figure 41. Spark Therapeutics Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 42. Ultragenyx Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 43. Shire PLC Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 44. Sangamo Therapeutics Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 45. Bioverativ Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 46. BioMarin Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 47. uniQure Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
Figure 48. Freeline Therapeutics Hemophilia Gene Therapy Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
